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Gastrointestinal ProblemsPhase 1/2BBTNCT02504554

Beneficial Bacteria Treatment for Autism

A Phase 1/2 study testing oral Vancomycin, MoviPrep and Prilosec in people with Gastrointestinal Problems and Autism Spectrum Disorders, run by Arizona State University.

Completed

Finished. The study has ended and is not enrolling. Results may be posted on the official record.

Official record
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Trial summary

This is an open-label clinical trial to investigate a combination therapy for treating gastrointestinal problems in children with autism spectrum disorders. The combination therapy includes beneficial bacteria. Read more about this study

Who is it for?
Ages 7 to 17 years
What is being tested?
oral Vancomycin, MoviPrep and Prilosec
Type of treatment
Pill or oral medicine
Could I receive a placebo?
No, everyone receives an active treatment
How many people
18 participants
Where
No sites listed yet
Study dates
Jul 2014to Apr 2016
Phase
Phase 1/2
Are there results?
Yes, posted in the registrySummary in the doctors' view

Key requirements

Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.

  • Ages 7 to 17 years
  • All sexes
  • No healthy volunteers
  • Child

Who may be able to join

  • Children ages 7-17 years
  • Diagnosis of autism per Autism Diagnostic Interview-Revised (ADI-R)
  • Moderate or Severe GI problems ( on the GSRS, a single score of 4 (severe) on any item, or a score of 3 (moderate) on two items, or a score of 2 (mild) or more on any 4 items
  • No changes in medications, supplements, diet, therapies, or education in last 3 months, and no intention to change them during clinical trial
  • General good physical health aside from gastrointestinal problems
  • Cognitive Ability to Provide Informed Assent

Who cannot join

  • Antibiotics in last 6 months
  • Probiotics in last 3 months
  • Single-gene disorder (Fragile X, etc.)
  • Major brain malformation
  • Tube feeding
  • Severe gastrointestinal problems that require immediate treatment (life-threatening)
Show all 10Show fewer
  • Ulcerative Colitis, Crohn's Disease, diagnosed Celiac Disease, Eosinophilic Gastroenteritis, or similar conditions
  • Severely underweight/malnourished
  • Recent or scheduled surgeries
  • Current participation in other clinical trials

About this study

Official title: Treating Gastrointestinal Problems in Children With Autism Using Beneficial Bacteria Treatment (BBT)

This is an open-label clinical trial to investigate a combination therapy for treating gastrointestinal problems in children with autism spectrum disorders.

The combination therapy includes beneficial bacteria.

Read the detailed description

This is an open-label clinical trial to evaluate the safety, tolerability, and feasibility of a combination therapy to treat gastrointestinal problems in children with autism spectrum disorders.

It involves a combination therapy including beneficial bacteria.

Being tested
oral Vancomycin, MoviPrep, Prilosec, human fecal material; processed, frozen administered orally, human fecal material; processed, frozen; administered orally and rectally
Keywords
children
Medical subject headings
Autism Spectrum Disorder

What participants receive

What participants receive. In a randomised study each person is assigned to one group by chance.

  • oral VancomycinDrug

    an antibiotic

  • MoviPrepDrug

    a bowel cleanse

  • PrilosecDrug

    a stomach acid suppressan

  • human fecal material; processed, frozen administered orallyBiological

    human fecal material; processed, frozen, administered orally

  • human fecal material; processed, frozen; administered orally and rectallyBiological

    human fecal material; processed, frozen; administered orally and rectally

Study groups in NCT02504554
Study groupRoleWhat they receive
Oral GroupExperimentalThis group will receive all treatments orally. The treatments include a combination of Vancomycin, MoviPrep, Prilosec, and human fecal material; processed, frozen.
Receives: Drug: oral Vancomycin; Drug: MoviPrep; Drug: Prilosec; Biological: human fecal material; processed, frozen administered orally
Rectal GroupExperimentalThis group will receive some treatments rectally and some orally. The treatments include a combination of Vancomycin, MoviPrep, Prilosec, and human fecal material; processed, frozen.
Receives: Drug: oral Vancomycin; Drug: MoviPrep; Drug: Prilosec; Biological: human fecal material; processed, frozen; administered orally and rectally

What is being measured

The primary outcome is the main question the study is designed to answer.

  1. Gastrointestinal Symptom Responsiveness Scale (GSRS)

    The GSRS is a measure of gastrointestinal symptoms. It includes 15 questions, rated on a Likert scale of 1-7, from no symptoms to severe symptoms, respectively (i.e., higher is worse). We report an average score for all 15 questions, so the possible range for the average score is also 1-7.

    Measured: Baseline and 10 weeks (end of treatment)

Secondary outcomes (7)
  1. Parent Global Impressions-Revised (PGI-R)

    The PGI-R is a rating of change of 18 autism symptoms compared to baseline, with each symptom rated on a Likert scale from -3 (much worse) to zero (no change) to +3 (much better). We report the average change of the 18 symptoms, so the possible range is from -3 to +3.

    Measured: Baseline and 10 weeks (end of treatment)

  2. Blood Safety Markers (Assessment of Blood Chemistry Panel and Complete Blood Count)

    Number of participants who had a clinically significant change in their blood safety markers (comprehensive metabolic panel including kidney/liver function and complete blood count with differential)

    Measured: Baseline and 10 weeks (end of treatment)

  3. Childhood Autism Rating Scale (CARS)

    The CARS is an assessment of 15 autism-related symptoms. Each item is scored on a scale of 1 (no symptoms) to 4 (severe symptoms), and the scores for each symptom are summed to obtain a total score. So, the possible scores range from 15 to 60, with a higher score indicating greater severity.

    Measured: Baseline and 10 weeks (end of treatment)

  4. Social Responsiveness Scale (SRS)

    The SRS is an assessment of social skills based on 65 items, where each item is scored on a range of 0 (no symptoms) to 3 (severe symptoms). The total score is a sum of the individual scores, so the total possible range is from 0 to 195, with a higher score indicating greater severity of symptoms.

    Measured: Baseline and 10 weeks (end of treatment)

  5. Short Sensory Profile

    The Short Sensory Profile is an assessment of sensory problems.

    However, the data on this scale was not collected due to administrative error.

    Measured: baseline and 10 weeks

  6. Vineland Adaptive Behavior Scale (VABS)

    The VABS is an assessment of adaptive behaviors, and we analyzed it to determine the developmental age of the participants, with possible scores ranging from 0 years to 21 years.

    Measured: baseline and 18 weeks (8 weeks after treatment stopped)

  7. Daily Stool Record (DSR)

    The DSR is a record of the type of stool that a participant had each day, using the Bristol Stool Form which ranges from 1 (very hard) to 7 (liquid). We then analyzed the data as % days of abnormal stools over a 14 day period, where an abnormal stool is defined as an unusually hard stool (types 1-2), unusually soft stool (types 6-7), or no stool that day. So, the possible range of % days of abnormal stools is from 0% to 100%, with a higher score indicating a more severe problem.

    Measured: Baseline and 10 weeks (end of treatment)

Timeline

From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.

  1. First posted22 Jul 2015 (estimated)
  2. Study startJul 2014
  3. Primary completionApr 2016
  4. Study completionApr 2016

Resources

More details

For doctors and researchers: how the study is designed, who runs it, and its registry IDs.

Study design
Study type
Interventional
Phase
Phase 1/2
Primary purpose
Treatment
Allocation
Non-randomised
Intervention model
Parallel groups
Masking
None (open label)
Enrolment
18 participants (actual)
IDs, dates and publications
ClinicalTrials.gov ID
NCT02504554
Sponsor's protocol ID
STUDY00001053
Acronym
BBT
Status last verified
Aug 2025
First submitted
30 Mar 2015
Last updated
12 Sep 2025
Data monitoring committee
Yes

Publications

  • Kang DW, Adams JB, Vargason T, Santiago M, Hahn J, Krajmalnik-Brown R. Distinct Fecal and Plasma Metabolites in Children with Autism Spectrum Disorders and Their Modulation after Microbiota Transfer Therapy. mSphere. 2020 Oct 21;5(5):e00314-20. doi: 10.1128/mSphere.00314-20.

    PubMed 33087514
  • Kang DW, Adams JB, Coleman DM, Pollard EL, Maldonado J, McDonough-Means S, Caporaso JG, Krajmalnik-Brown R. Long-term benefit of Microbiota Transfer Therapy on autism symptoms and gut microbiota. Sci Rep. 2019 Apr 9;9(1):5821. doi: 10.1038/s41598-019-42183-0.

    PubMed 30967657
  • Kang DW, Adams JB, Gregory AC, Borody T, Chittick L, Fasano A, Khoruts A, Geis E, Maldonado J, McDonough-Means S, Pollard EL, Roux S, Sadowsky MJ, Lipson KS, Sullivan MB, Caporaso JG, Krajmalnik-Brown R. Microbiota Transfer Therapy alters gut ecosystem and improves gastrointestinal and autism symptoms: an open-label study. Microbiome. 2017 Jan 23;5(1):10. doi: 10.1186/s40168-016-0225-7.

    PubMed 28122648

Questions about this trial

What is this clinical trial studying?

A Phase 1/2 study testing oral Vancomycin, MoviPrep and Prilosec in people with Gastrointestinal Problems and Autism Spectrum Disorders, run by Arizona State University.

The full registered description is in the About this study section and the official record.

Who may be eligible to take part?

The sponsor lists 6 inclusion and 10 exclusion criteria. Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.

Is this clinical trial currently recruiting?

The record says: finished, as of the sponsor's last update on 12 Sep 2025. Status can change between updates, so confirm with the study contact before making plans.

What are the possible benefits and risks?

They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.

What does this combined phase mean?

Phase 1 studies test a treatment in a small group of people for the first time or in a new way, mainly to check safety and find the right dose.

Phase 2 studies give the treatment to a larger group to see whether it has the intended effect and to keep checking safety.

Not every study follows the same path, and some studies (observational studies, device studies) have no phase.

Are results available for this study?

Yes. Results are posted in the registry (first posted 18 Dec 2019). A summary is in the For doctors view, and the full results are on ClinicalTrials.gov.

How can a doctor refer a patient or contact the research team?

The record lists no contact. The official record names the sponsor, who can be asked directly. AzTrials does not enrol participants or take referrals.

What does the primary outcome measure?

Gastrointestinal Symptom Responsiveness Scale (GSRS) (time frame: Baseline and 10 weeks (end of treatment)). It is what the study was designed to measure, not a finding.

Where can I read the original study information?

On the ClinicalTrials.gov record for NCT02504554, which also lists 3 linked publications.

Does a listing mean the treatment is approved or proven to work?

No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.

How often is this information updated?

AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 12 Sep 2025.

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