AzTrials
AzTrials

Immune ThrombocytopeniaPhase 3NCT02859909

This Clinical Study is to Test Efficacy and Safety of BT595 in Chronic Primary Immune Thrombocytopenia (ITP)

A Phase 3 study testing BT595 in people with Immune Thrombocytopenia, run by Biotest at 22 sites in 6 countries.

Completed

Finished. The study has ended and is not enrolling. Results may be posted on the official record.

Official record
Search all trials

Trial summary

The main purpose of this study is to assess the efficacy and safety of BT595 in adult subjects with chronic ITP. The primary objective of this study is to determine the rate of subjects with a response. Read more about this study

Who is it for?
Ages 18 to 75 years
Conditions the study is for
Immune Thrombocytopenia
What is being tested?
BT595
Could I receive a placebo?
No, everyone receives an active treatment
How many people
34 participants
Where
22 sitesin 6 countries
Study dates
Nov 2016to Dec 2018
Phase
Phase 3
Are there results?
None posted in the registry

Key requirements

Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.

  • Ages 18 to 75 years
  • All sexes
  • No healthy volunteers
  • Adult, Older adult

Main Inclusion Criteria:

  • Diagnosis of chronic ITP (>12 months' duration), including diagnosis of refractory ITP, and as defined by the International Working Group (Rodeghiero et al, 2009), where ITP is described as an autoimmune disorder characterized by isolated thrombocytopenia in the absence of other causes or disorders that may be associated with thrombocytopenia
  • Treatment is indicated because of a high risk of bleeding or a need to raise the platelet count
  • Mean screening platelet count of <30×10^9/L from 3 qualifying platelet counts performed within approximately 7 to 14 days before the start of treatment, with no individual platelet count above 35×10^9/L. The subject may be rescreened if the mean screening platelet count is ≥30×10^9/L. (Note: If a subject is rescreened, all screening laboratory tests must be repeated.)

Main Exclusion Criteria:

  • Secondary thrombocytopenia or acquired medical conditions known to be associated with secondary thrombocytopenia, such as chronic lymphocytic leukemia; lymphoma; multiple myeloma; thyroid disease; or other forms of thrombocytopenia, such as drug induced thrombocytopenia; cirrhotic liver diseases; antiphospholipid syndrome; environmental thrombocytopenia; and bone marrow diseases
  • Severe concomitant diseases that in the judgment of the investigator will interfere with the study, such as autoimmune hemolytic anemia, acute renal failure, and noncontrolled arterial hypertension
  • Laboratory findings (e.g., abnormal laboratory values for hemoglobin, transaminase levels [alanine aminotransferase, aspartate aminotransferase], total bilirubin, creatinine, blood urea nitrogen, and immunoglobulins G, A, M) that preclude participation
  • Positive Coombs test (direct and indirect)
  • Planned invasive procedures during the time frame of the study
  • Maintenance therapy with intravenous immunoglobulins (IVIgs) or infusion of IVIgs within 3 months before start of the study
  • Unresponsive to previous IVIg treatment
  • Additional therapy with high dose corticosteroids (equivalent to >30 mg prednisone/day), thrombopoietin receptor agonists, and/or immunosuppressives and/or other therapies (e.g., infusion of platelets) within 1 month before the start of the study (Note: Subjects on stable doses of ITP active treatment must not have modified the dose in the preceding 2 weeks and must maintain their prestudy dose during the study. Corticosteroids should not be given as a premedication. Rescue therapy with short courses [i.e., 1 to 4 days] of high dose steroids and IVIgs are allowed up to 2 weeks before study inclusion.)
  • History of thrombotic events (including myocardial infarction, cerebral vascular accident [including stroke], pulmonary embolism, and deep vein thrombosis) 6 months before treatment start with BT595 or the presence of significant risk factors for thrombotic events
  • Therapy with live attenuated virus vaccines 3 months before start of the study
  • Selective, absolute immunoglobulin A (IgA) deficiency or known antibodies to IgA

Trial locations and contacts

22 sites in 6 countries.

22 sites in 6 countries

Hungary6 sites
  • Investigational site # 3601

    Budapest, 1083

  • Investigational site # 3604

    Debrecen, 4032

  • Investigational site # 3607

    Győr, 9023

  • Investigational site # 3602

    Miskolc, 3529

  • Investigational site # 3603

    Nyíregyháza, 4400

  • Investigational site # 3606

    Pécs, 7621

Other trials in Hungary

Bulgaria5 sites
  • Investigational site # 3597

    Pleven, 5800

  • Investigational site # 3593

    Plovdiv, 4000

  • Investigational site # 3598

    Sofia, 1431

  • Investigational site # 3591

    Sofia, 1756

  • Investigational site # 3596

    Varna, 9010

Other trials in Bulgaria

Serbia4 sites
  • Investigational site # 3811

    Belgrade, 11000

  • Investigational site # 3813

    Belgrade, 11080

  • Investigational site #3814

    Niš, 18000

  • Investigational site # 3812

    Novi Sad, 21000

Other trials in Serbia

Spain4 sites
  • Investigational site # 3403

    Madrid, 28006

  • Investigational site # 3404

    Madrid, 28007

  • Investigational site #3401

    Málaga

  • Investigational site # 3402

    Palma de Mallorca, 07012

Other trials in Spain

Germany2 sites
  • Investigational site # 4901

    Berlin, 13353

  • Investigational Site #4902

    München, 81377

Other trials in Germany

Czechia1 site
  • Investigational site # 4202

    Prague, 10034

Other trials in Czechia

About this study

Official title: An Open Label, Prospective, Randomized, Multicenter Study Investigating Clinical Efficacy and Safety of the Human Normal Immunoglobulin for Intravenous Administration BT595 in Patients With Chronic Primary Immune Thrombocytopenia (ITP)

The main purpose of this study is to assess the efficacy and safety of BT595 in adult subjects with chronic ITP. The primary objective of this study is to determine the rate of subjects with a response. A response is defined as a platelet count of ≥30×10^9/L and at least a 2 fold increase of the baseline count, confirmed on at least 2 separate occasions at least 7 days apart, and the absence of bleeding. The secondary objectives of this study, in addition to further efficacy assessments, are to evaluate the safety of BT595.

Being tested
BT595
Medical subject headings
Purpura, Thrombocytopenic, Idiopathic

What participants receive

What participants receive. In a randomised study each person is assigned to one group by chance.

  • BT595Biological

    Also called Human Immunoglobulin

Study groups in NCT02859909
Study groupRoleWhat they receive
2 day treatment scheduleExperimentalPatients will receive a dosage of 1 g/kg bw per day of BT595 for 2 consecutive days
Receives: Biological: BT595
5 day treatment scheduleExperimentalPatients will receive a dosage of 0.4 g/kg bw per day of BT595 for 5 consecutive days
Receives: Biological: BT595

What is being measured

The primary outcome is the main question the study is designed to answer.

  1. Rate of subjects with response (R)

    The rate of subjects with response is defined as subjects with a platelet count of ≥30×10^9/L and at least a 2 fold increase of the baseline count, confirmed on at least 2 separate occasions at least 7 days apart, and the absence of bleeding

    Measured: 1 month

Secondary outcomes (14)
  1. The number of subjects with complete response (CR)

    The number of subjects with CR, which is defined as a platelet count ≥100×10^9/L, confirmed on at least 2 separate occasions at least 7 days apart, and the absence of bleeding

    Measured: 1 month

  2. The percentage of subjects with complete response (CR)

    The percentage of subjects with CR, which is defined as a platelet count ≥100×10^9/L, confirmed on at least 2 separate occasions at least 7 days apart, and the absence of bleeding

    Measured: 1 month

  3. The number of subjects with no response (NR)

    The number of subjects with NR, which is defined as subjects without R, i.e. a platelet count <30×10^9/L or less than a 2 fold increase of baseline platelet count, confirmed on at least 2 separate occasions, approximately 1 day apart, or bleeding

    Measured: 1 month

  4. The percentage of subjects with no response (NR)

    The percentage of subjects with NR, which is defined as subjects without R, i.e. a platelet count <30×10^9/L or less than a 2 fold increase of baseline platelet count, confirmed on at least 2 separate occasions, approximately 1 day apart, or bleeding

    Measured: 1 month

  5. The number of subjects with a loss of response

    The number of subjects with a loss of response (only in subjects who previously had CR or R), which is defined as a platelet count <100×10^9/L or bleeding (from CR) or platelet count <30×10^9/L or less than 2 fold increase of the baseline platelet count, or bleeding (from R). Platelet counts will be confirmed on at least 2 separate occasions approximately 1 day apart

    Measured: 1 month

  6. The percentage of subjects with a loss of response

    The percentage of subjects with a loss of response (only in subjects who previously had CR or R), which is defined as a platelet count <100×10^9/L or bleeding (from CR) or platelet count <30×10^9/L or less than 2 fold increase of the baseline platelet count, or bleeding (from R). Platelet counts will be confirmed on at least 2 separate occasions approximately 1 day apart

    Measured: 1 month

  7. Time to Response (R)

    Time to response (R), which is defined as the time from the start of treatment to the time of achievement of CR or R

    Measured: 1 month

  8. Duration of response (R),

    Duration of response (R), which is defined as the time from the achievement of CR or R to loss of CR or R

    Measured: 1 month

  9. The number of subjects with response to ≥50×10^9/L

    The number of subjects with response to ≥50×10^9/L, which is defined as a platelet count increase to at least ≥50×10^9/L within 7 days of the first BT595 infusion

    Measured: 1 month

  10. The percentage of subjects with response to ≥50×10^9/L

    The percentage of subjects with response to ≥50×10^9/L, which is defined as a platelet count increase to at least ≥50×10^9/L within 7 days of the first BT595 infusion

    Measured: 1 month

  11. Subject's maximum platelet count achieved

    Measured: 1 month

  12. Time to subject's maximum platelet count

    Measured: 1 month

  13. Time course of platelet count

    Measured: 1 month

  14. Occurrence of bleeding symptoms

    Measured: 1 month

Timeline

From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.

  1. First posted9 Aug 2016 (estimated)
  2. Study startNov 2016
  3. Primary completionDec 2018
  4. Study completionDec 2018

Resources

More details

For doctors and researchers: how the study is designed, who runs it, and its registry IDs.

Study design
Study type
Interventional
Phase
Phase 3
Primary purpose
Treatment
Allocation
Randomised
Intervention model
Parallel groups
Masking
None (open label)
Enrolment
34 participants (actual)
IDs, dates and publications
ClinicalTrials.gov ID
NCT02859909
Sponsor's protocol ID
992
Status last verified
Apr 2018
First submitted
25 Jul 2016
Last updated
14 Aug 2019
Results posted
No
Data monitoring committee
Yes
Individual data sharing
Undecided

Publications

  • Demeter J, Hamed A, Laszlo S, Suvajdzic N, Aigner S, Borner B, Staiger C. Efficacy and safety of BT595 (10% human intravenous immunoglobulin) in adult patients with chronic immune thrombocytopenia. Transfus Med. 2023 Apr;33(2):165-173. doi: 10.1111/tme.12943. Epub 2022 Nov 30.

    PubMed 36448274

Questions about this trial

What is this clinical trial studying?

A Phase 3 study testing BT595 in people with Immune Thrombocytopenia, run by Biotest at 22 sites in 6 countries.

The full registered description is in the About this study section and the official record.

Who may be eligible to take part?

Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.

Is this clinical trial currently recruiting?

The record says: finished, as of the sponsor's last update on 14 Aug 2019. Status can change between updates, so confirm with the study contact before making plans.

Where is the study taking place?

The record lists 22 sites in Hungary, Bulgaria, Serbia, Spain, Germany and 1 more country. Whether a site is taking part right now should be confirmed with that site. See every site.

What are the possible benefits and risks?

They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.

What does this phase mean?

Phase 3 studies compare the treatment with the current standard treatment or a placebo in a large group, to confirm how well it works and watch for side effects.

Not every study follows the same path, and some studies (observational studies, device studies) have no phase.

Are results available for this study?

The study is completed, but results are not available in the source record. That does not mean the treatment did or did not work.

How can a doctor refer a patient or contact the research team?

The record lists no contact. The official record names the sponsor, who can be asked directly. AzTrials does not enrol participants or take referrals.

What does the primary outcome measure?

Rate of subjects with response (R) (time frame: 1 month). It is what the study was designed to measure, not a finding.

Where can I read the original study information?

On the ClinicalTrials.gov record for NCT02859909, which also lists 1 linked publication.

Does a listing mean the treatment is approved or proven to work?

No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.

How often is this information updated?

AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 14 Aug 2019.

Free account

Keep searching with a free account

You’ve used your 3 free searches for this session. Log in or create a free AzTrials account to keep searching clinical trials and save the ones you want to follow.

Create a free accountLog in