Myotonic Dystrophy Type 1NCT06316778
Pelvic Floor Muscle Training for Women with Myotonic Dystrophy
A study testing Pelvic floor muscle training in people with Myotonic Dystrophy Type 1 and Urinary Incontinence, run by Université de Sherbrooke at 1 site in Canada.
Trial summary
Myotonic dystrophy type 1 (DM1) is a neuromuscular disease characterized by multisystem manifestations. DM1 can affect the urinary system through the impact of the pelvic floor muscles (PFM). Read more about this study
- Who is it for?
- Ages 18 years and older, women only
- Conditions the study is for
- Myotonic Dystrophy Type 1, Urinary Incontinence
- What is being tested?
- Pelvic floor muscle training
- Type of treatment
- Lifestyle or therapy programme
- Could I receive a placebo?
- No, everyone receives an active treatment
- How many people
- 12 participants
- Where
- 1 siteCanada
- Study dates
- 11 Mar 2024to 30 Dec 2026
- Phase
- Interventional
- Are there results?
- Not yet: the study is under way
Key requirements
Who can take part, as listed by the sponsor. Only the study team can confirm whether you are eligible, so take this list to your doctor.
- Ages 18 years and older
- Women only
- No healthy volunteers
- Adult, Older adult
Who may be able to join
- confirmed medical diagnosis of myotonic dystrophy type 1 (DM1) with adult phenotype
- symptoms of stress, urge or mixed urinary incontinence
- able to give a free and informed consent
Who cannot join
- being pregnant, have given birth by vaginal delivery in the last year or plan to become pregnant in the next six months
- present post-void residual urine ≥ 150 ml
- have medical conditions that may have an impact on the symptoms of urinary incontinence and the response to treatments
- present fecal incontinence (≥ 1/week) or significant prolapse (beyond the hymen)
- have already received physiotherapy treatments in pelvic floor rehabilitation or surgery on the perineum
- have a defibrillator, pacemaker or bladder stimulator
Trial locations and contacts
1 site in 1 country. Contact the study team or a site near you to ask about taking part.
Canada1 site, 1 recruiting
- Recruiting
Clinique des maladies neuromusculaires
Jonquière, Quebec, G7X 7X2
Mélanie Morin, PhD, 819-346-1110 ext. 13818, melanie.m.morin@usherbrooke.ca
Cynthia Gagnon, PhD, 418-695-7700 ext. 2756, Cynthia.gagnon4@usherbrooke.ca
About this study
Official title: Pelvic Floor Muscle Training for Urinary Incontinence in Women with Myotonic Dystrophy Type 1: a Feasibility and Acceptability Study
Myotonic dystrophy type 1 (DM1) is a neuromuscular disease characterized by multisystem manifestations. DM1 can affect the urinary system through the impact of the pelvic floor muscles (PFM). Urinary incontinence can occur in this situation and is often offset with compensatory measures without restoring the PFM function (e.g. sanitary pads). PFM training have already been shown to be effective in reducing or even eliminating urinary incontinence in the general population. However, no study has been the subject of this modality in people with DM1. Having recently shown that it is possible to gain strength with DM1, a strengthening protocol targeting PFM could prove effective in treating urinary incontinence. The objectives of this study are i) to assess the feasibility and acceptability of PFM training and ii) to investigate the effects of PFM training in women with DM1 with adult phenotype. A quasi-experimental study will be conducted with 12 women having a confirmed diagnosis of DM1 with urinary incontinence. Participants will follow a 12-week PFM training program, comprising weekly sessions with an experienced physiotherapist as well as a home exercise program. Outcomes measures will be assessed at baseline and at post-treatment and will include: feasibility and acceptability variables, frequency of urinary incontinence, urogynecological symptoms and their impact on quality of life, morphometry and function of PFM, and the perceived improvement following the treatments. This study has the potential to improve the management of urinary incontinence and support the implementation of pelvic floor rehabilitation services in this population.
- Conditions
- Myotonic Dystrophy Type 1, Urinary Incontinence
- Being tested
- Pelvic floor muscle training
- Keywords
- Neuromuscular disease, Physiotherapy, Exercises, Urinary incontinence
- Medical subject headings
- Myotonic Dystrophy, Urinary Incontinence, Neuromuscular Diseases, Motor Activity
What participants receive
What participants receive. In a randomised study each person is assigned to one group by chance.
Pelvic floor muscle trainingBehavioural
12 weekly sessions of 60 minutes with an experienced physiotherapist, including pelvic floor muscles (PFM) exercises with biofeedback, teaching home exercises and education.
| Study group | Role | What they receive |
|---|---|---|
| Pelvic floor muscle training | Experimental | Not described Receives: Behavioral: Pelvic floor muscle training |
What is being measured
The primary outcome is the main question the study is designed to answer.
Percentage of attended treatment sessions
To determine feasibility, the patients' adherence to treatment sessions will be recorded (present vs absent) as well as reasons for non-attendance.
Measured: Through treatment completion (session 1 to 12; 12 weeks of treatment)
Percentage of home exercises performed
- The adherence rate to home exercises for each treatment group will be assessed using a daily diary. The participants will record the frequency of the exercises completed.
- To determine feasibility by assessing adherence to treatment sessions.
Measured: Through treatment completion (session 1 to 12; 12 weeks of treatment)
Retention rate
To determine feasibility by assessing the percentage of participants completing the post-treatment assessment. Reason for dropouts will be compiled.
Measured: Baseline to Post-treatment assessment (2-week post-treatment)
Recruitment rate
To determine feasibility by assessing the percentage of participants included versus the participants screened. The barriers and reasons for refusing to participate as well as the reasons for exclusion will be documented.
Measured: Baseline
Intervention Acceptability Questionnaire
The Intervention Acceptability Questionnaire will be used to assess the participants' acceptability of the interventions. This questionnaire consists of 4 items measured on a VAS scale (Minimum value: 0; Maximum Value: 10). Each item is analyzed separately, with a greater score meaning higher acceptability of the intervention. This outcome measure will contribute to identifying factors limiting the acceptability of each program.
Measured: At baseline and after 12 weeks of treatment
Secondary outcomes (9)
Change in the frequency of urinary incontinence episodes
Evaluated with the 7-day bladder diary (number of leak/week).
Measured: Baseline to post-treatment (after the 12-week program)
Change in urinary incontinence symptoms
Evaluated with the International Consultation Incontinence Questionnaire (ICIQ-UI-SF) Ranging from 0 to 21, higher scores indicate worse outcome (more urinary incontinence symptoms and a higher impact on their quality of life).
Measured: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor disorder symptoms
Evaluated with the Pelvic Floor Disorder Inventory (PFDI). Ranging from 0 to 300, higher scores indicate worse outcome (more pelvic floor disorder symptoms).
Measured: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor disorder symptoms related impact on quality of life
Evaluated with the Pelvic Floor Impact Questionnaire (PFIQ-SF). Ranging from 0 to 300, higher scores indicate a worse outcome (higher impact on their quality of life).
Measured: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor muscles morphometry
Evaluated with transperineal ultrasound.
Measured: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor muscles function
Evaluated with dynamometry.
Measured: Baseline to post-treatment (after the 12-week program)
Patient's satisfaction
Evaluated with Patient satisfaction questionnaire (PSQ) ranging from "completely satisfied" to "not satisfied at all".
Measured: Post-treatment (after the 12-week program)
Patient's global impression of change
Evaluated with Patients' Global Impression of Improvement (PGI-I). Ranging from 1 "very much better" to 7 "very much worse" on a 7-point likert scale.
Measured: Post-treatment (after the 12-week program)
Patient's estimated improvement
Evaluated with Estimated percent improvement (EPI). Ranging from 0 "no amelioration" to 100 "complete amelioration".
Measured: Post-treatment (after the 12-week program)
Timeline
From the start of the study to its completion; the mark is today. Estimated dates are the sponsor’s plan.
- First posted18 Mar 2024
- Study start11 Mar 2024
- Primary completion30 Dec 2026 (estimated)
- Study completion30 Dec 2026 (estimated)
Resources
- Official record on ClinicalTrials.govThe registry entry this page is built from, with its full change history.
- Other trials for Myotonic Dystrophy Type 1Studies of the same condition, open and under way.
- More trials run by Université de SherbrookeThe sponsor's other registered studies.
- What the trial phases meanHow a treatment moves from first tests in people to approval.
More details
For doctors and researchers: how the study is designed, who runs it, and its registry IDs.
Study design
- Study type
- Interventional
- Phase
- Phase N/A
- Primary purpose
- Treatment
- Allocation
- Not applicable
- Intervention model
- Single group
- Model description
- pre-treatment assessment - intervention (12 weeks) - post-treatment assessment
- Masking
- None (open label)
- Enrolment
- 12 participants (estimated)
Sponsor and investigators
- Lead sponsor
- Université de Sherbrooke
- Sponsor type
- University, hospital or other
- Collaborators
- Centre de recherche du Centre hospitalier universitaire de Sherbrooke, Interdisciplinary research team on neuromuscular diseases (GRIMN), CIUSSS Saguenay-Lac-Saint-Jean
- Responsible party
- Principal investigator, Mélanie Morin, Université de Sherbrooke
IDs, dates and publications
- ClinicalTrials.gov ID
- NCT06316778
- Sponsor's protocol ID
- 2023-038
- Status last verified
- Feb 2025
- First submitted
- 7 Mar 2024
- Last updated
- 24 Feb 2025
- Results posted
- No
- Data monitoring committee
- No
- FDA-regulated drug
- No
- FDA-regulated device
- No
Study at a glance
From the registry record, last updated by the sponsor on 24 Feb 2025. Recruitment status is as the sponsor reported it: confirm with the study team.
- Official title
- Pelvic Floor Muscle Training for Urinary Incontinence in Women with Myotonic Dystrophy Type 1: a Feasibility and Acceptability Study
- ClinicalTrials.gov ID
- NCT06316778
- Acronym / sponsor ID
- 2023-038
- Conditions
- Myotonic Dystrophy Type 1, Urinary Incontinence
- Keywords
- Neuromuscular disease, Physiotherapy, Exercises, Urinary incontinence
- Study type
- Interventional
- Recruitment status
- Recruiting
- Enrolment
- 12 participants (estimated)
- Lead sponsor
- Université de SherbrookeUniversity, hospital or other
- Collaborators
- Centre de recherche du Centre hospitalier universitaire de Sherbrooke, Interdisciplinary research team on neuromuscular diseases (GRIMN), CIUSSS Saguenay-Lac-Saint-Jean
- Study start
- 11 Mar 2024 (actual)
- Primary completion
- 30 Dec 2026 (estimated)
- Study completion
- 30 Dec 2026 (estimated)
- First posted
- 18 Mar 2024 (actual)
- Results
- Not posted in the source record
Clinical summary
The research question as the sponsor registered it. This describes what the study plans to test, not what it found.
Myotonic dystrophy type 1 (DM1) is a neuromuscular disease characterized by multisystem manifestations. DM1 can affect the urinary system through the impact of the pelvic floor muscles (PFM). Urinary incontinence can occur in this situation and is often offset with compensatory measures without restoring the PFM function (e.g. sanitary pads). PFM training have already been shown to be effective in reducing or even eliminating urinary incontinence in the general population. However, no study has been the subject of this modality in people with DM1. Having recently shown that it is possible to gain strength with DM1, a strengthening protocol targeting PFM could prove effective in treating urinary incontinence. The objectives of this study are i) to assess the feasibility and acceptability of PFM training and ii) to investigate the effects of PFM training in women with DM1 with adult phenotype. A quasi-experimental study will be conducted with 12 women having a confirmed diagnosis of DM1 with urinary incontinence. Participants will follow a 12-week PFM training program, comprising weekly sessions with an experienced physiotherapist as well as a home exercise program. Outcomes measures will be assessed at baseline and at post-treatment and will include: feasibility and acceptability variables, frequency of urinary incontinence, urogynecological symptoms and their impact on quality of life, morphometry and function of PFM, and the perceived improvement following the treatments. This study has the potential to improve the management of urinary incontinence and support the implementation of pelvic floor rehabilitation services in this population.
Study design
- Primary purpose
- Treatment
- Allocation
- Not applicable
- Intervention model
- Single group
- Masking
- None (open label)
- Number of arms
- 1
- Model description
- pre-treatment assessment - intervention (12 weeks) - post-treatment assessment
| Arm | Type | Receives |
|---|---|---|
| Pelvic floor muscle training | Experimental | Behavioral: Pelvic floor muscle training |
Who may qualify
- Ages
- 18 years and older
- Sex
- Female only
- Healthy volunteers
- Not accepted
- Age groups
- Adult, Older adult
Key inclusion criteria (3 listed)
- confirmed medical diagnosis of myotonic dystrophy type 1 (DM1) with adult phenotype
- symptoms of stress, urge or mixed urinary incontinence
- able to give a free and informed consent
Key exclusion criteria (6 listed)
- being pregnant, have given birth by vaginal delivery in the last year or plan to become pregnant in the next six months
- present post-void residual urine ≥ 150 ml
- have medical conditions that may have an impact on the symptoms of urinary incontinence and the response to treatments
- present fecal incontinence (≥ 1/week) or significant prolapse (beyond the hymen)
- have already received physiotherapy treatments in pelvic floor rehabilitation or surgery on the perineum
Eligibility is decided by the study team after screening; this overview does not establish that a patient qualifies. Full inclusion and exclusion criteria.
Interventions
| Intervention | Type | Arms |
|---|---|---|
| Pelvic floor muscle training12 weekly sessions of 60 minutes with an experienced physiotherapist, including pelvic floor muscles (PFM) exercises with biofeedback, teaching home exercises and education. | Behavioural | Pelvic floor muscle training |
Primary outcome
Percentage of attended treatment sessions
Time frame: Through treatment completion (session 1 to 12; 12 weeks of treatment)
To determine feasibility, the patients' adherence to treatment sessions will be recorded (present vs absent) as well as reasons for non-attendance.
Percentage of home exercises performed
Time frame: Through treatment completion (session 1 to 12; 12 weeks of treatment)
1. The adherence rate to home exercises for each treatment group will be assessed using a daily diary. The participants will record the frequency of the exercises completed. 2. To determine feasibility by assessing adherence to treatment sessions.
Retention rate
Time frame: Baseline to Post-treatment assessment (2-week post-treatment)
To determine feasibility by assessing the percentage of participants completing the post-treatment assessment. Reason for dropouts will be compiled.
Recruitment rate
Time frame: Baseline
To determine feasibility by assessing the percentage of participants included versus the participants screened. The barriers and reasons for refusing to participate as well as the reasons for exclusion will be documented.
Intervention Acceptability Questionnaire
Time frame: At baseline and after 12 weeks of treatment
The Intervention Acceptability Questionnaire will be used to assess the participants' acceptability of the interventions. This questionnaire consists of 4 items measured on a VAS scale (Minimum value: 0; Maximum Value: 10). Each item is analyzed separately, with a greater score meaning higher acceptability of the intervention. This outcome measure will contribute to identifying factors limiting the acceptability of each program.
9 secondary outcomes
Change in the frequency of urinary incontinence episodes
Time frame: Baseline to post-treatment (after the 12-week program)
Change in urinary incontinence symptoms
Time frame: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor disorder symptoms
Time frame: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor disorder symptoms related impact on quality of life
Time frame: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor muscles morphometry
Time frame: Baseline to post-treatment (after the 12-week program)
Change in pelvic floor muscles function
Time frame: Baseline to post-treatment (after the 12-week program)
Patient's satisfaction
Time frame: Post-treatment (after the 12-week program)
Patient's global impression of change
Time frame: Post-treatment (after the 12-week program)
Patient's estimated improvement
Time frame: Post-treatment (after the 12-week program)
Results and safety
This study is still under way. Results are not available in the source record yet.
Research links
- Official record on ClinicalTrials.govLast updated by the sponsor 24 Feb 2025.
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Referral and contact
AzTrials does not enrol participants or take referrals. Contact the study team or a site listed below; they decide who can take part.
Clinique des maladies neuromusculaires
Jonquière, Canada
1 site in 1 country: see every site and its status.
Questions about this trial
What is this clinical trial studying?
A study testing Pelvic floor muscle training in people with Myotonic Dystrophy Type 1 and Urinary Incontinence, run by Université de Sherbrooke at 1 site in Canada.
The full registered description is in the About this study section and the official record.
Who may be eligible to take part?
The sponsor lists 3 inclusion and 6 exclusion criteria. Eligibility is decided by the study team after screening, so read the full criteria and contact a listed site.
Is this clinical trial currently recruiting?
The record says: looking for participants now, as of the sponsor's last update on 24 Feb 2025. Status can change between updates, so confirm with the study contact before making plans.
Where is the study taking place?
The record lists 1 site in Canada. Whether a site is taking part right now should be confirmed with that site. See every site.
What are the possible benefits and risks?
They depend on the study and the treatment, and no study can promise a benefit. The study team explains the known risks during informed consent, before anyone joins; the record itself does not list them.
Are results available for this study?
This study is still under way. Results are not available in the source record yet.
How can a doctor refer a patient or contact the research team?
Each site lists its own contact: choose the nearest one under Trial locations. AzTrials does not enrol participants or take referrals.
What does the primary outcome measure?
Percentage of attended treatment sessions (time frame: Through treatment completion (session 1 to 12; 12 weeks of treatment)). The study lists 5 primary outcomes in all. It is what the study was designed to measure, not a finding.
Where can I read the original study information?
Does a listing mean the treatment is approved or proven to work?
No. A listing means the study is registered. It does not show that the treatment is safe, works, or is approved by a regulator.
How often is this information updated?
AzTrials copies changed records from ClinicalTrials.gov every night and reloads the whole registry every week. The sponsor last updated this record on 24 Feb 2025.