Clinical trials: DMD, open to volunteers

Duchenne Muscular Dystrophy

A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy

• Recruiting
• Age: 4 to 9 years
• Phase 1/2

The study will evaluate the tolerability, safety and efficacy of gene therapy product in boys with Duchenne muscular dystrophy (DMD).

Trial name

NCT07673809

Testing

GNR-097

Where

6 sites in Belarus, Russia

Volunteers

32 people

Sponsor

AO GENERIUM