Clinical trials: Glutaric Aciduria Type I
Glutaric Acidemia Type I, Glutaric Aciduria Type I
A Study to Evaluate the Tolerability, Safety and Efficacy of VGM-R02b
Phase I, open-label, single-arm, single-dose, trial of VGM-R02b (gene replacement therapy) in patients with Glutaric Acidemia Type I (GA-I) who meet enrollment criteria and are genetically confirmed by GCDH gene mutation.
- Trial name
- NCT06217861
- Testing
- VGM-R02b
- Where
- China
- Volunteers
- 12 people
- Sponsor
- Shanghai Vitalgen BioPharma Co., Ltd.