Clinical trials: Hereditary Tyrosinemia

Tyrosinemia I

Study of NTBC for Tyrosinemia I

• Completed
• Age: Up to 17 years

OBJECTIVES: I. Assess the safety and efficacy of NTBC in children with tyrosinemia I. II. Evaluate the effects of NTBC on survival, rate of neurologic crises, improvement in renal tubular damage, reduction in the need for liver…

Trial name

NCT00004443

Testing

NTBC

Where

3 sites in United States, Canada

Volunteers

20 people

Sponsor

University of Washington