Clinical trials: Hyper-IgM Syndrome

Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

• Recruiting
• Age: 2 months to 60 years
• Observational study

This is a data collection study that will examine the general diagnostic and treatment data associated with the reduced-intensity chemotherapy-based regimen paired with simple alemtuzumab dosing strata designed to prevented graft…

Conditions

Primary Immunodeficiency (PID), Congenital Bone Marrow Failure Syndromes, Inherited Metabolic Disorders (IMD), Hereditary Anemias

Trial name

PRO-RIC (NCT04528355)

Testing

data collection

Where

United States

Volunteers

50 people

Sponsor

Paul Szabolcs