Clinical trials: Leber Hereditary Optic Neuropathy (LHON)

Leber Hereditary Optic Neuropathy

RESCUE and REVERSE Long-term Follow-up

• Completed
• Age: 15 years and older
• Phase 3
• Results posted

The goal of this clinical trial is to assess the long-term safety and efficacy of GS010, a gene therapy, and assess the quality of life in subjects with LHON due to the G11778A ND4 mitochondrial mutation and who were treated in…

Trial name

RESTORE (NCT03406104)

Testing

GS010

Where

7 sites in United States, France and 3 more

Volunteers

62 people

Sponsor

GenSight Biologics