Clinical trials: Phelan-McDermid Syndrome
- Condition Phelan-McDermid Syndrome
- Funder type Industry (pharma, biotech, devices)
- Has posted results yes
Phelan-McDermid Syndrome
An Open-Label Study of Oral NNZ-2591 in Phelan-McDermid Syndrome (PMS-001)
A study of the safety, tolerability and pharmacokinetics of NNZ-2591 and measures of efficacy in children and adolescents with Phelan-McDermid Syndrome.
- Trial name
- PMS-001 (NCT05025241)
- Testing
- NNZ-2591
- Where
- 4 sites in United States
- Volunteers
- 18 people
- Sponsor
- Neuren Pharmaceuticals Limited