Clinical trials: Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]

Infantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]

Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients

• Unknown status
• Age: 5 to 12 months
• Phase 1/2

Spinal Muscular Atrophy (SMA) is an autosomal recessive disease of motor neurons. In the early 1980s, Werdnig from Vienna University and Hoffman from Heidelberg University described this disorder.

Trial name

NCT02855112

Testing

Adipose derived mesenchymal stem cell

Where

Iran

Volunteers

10 people

Sponsor

Tehran University of Medical Sciences