Clinical trials: Moderate Aplastic Anemia Requiring Transfusions
Idiopathic Aplastic Anemia, Severe Aplastic Anemia
Up-front Matched Unrelated Donor Transplantation in Pediatric Patients With Idiopathic Aplastic Anemia
Pediatric patients with idiopathic aplastic anemia (AA) respond better than adults to immunosuppressive therapy (IST) but the long-term risks of relapse, ciclosporine dependence, and clonal evolution are high.
- Conditions
- Idiopathic Aplastic Anemia, Severe Aplastic Anemia, Moderate Aplastic Anemia Requiring Transfusions
- Trial name
- UPFRONT-MUD (NCT05419843)
- Testing
- HSCT Arm group
- Volunteers
- 25 people
- Sponsor
- Assistance Publique - Hôpitaux de Paris